Gene Therapy

Gene Therapy, Published online: 04 May 2026; doi:10.1038/s41434-026-00618-0 Clinical response to systemic AAV gene therapy in a large animal model of late-stage lysosomal storage disease

Gene Therapy, Published online: 30 April 2026; doi:10.1038/s41434-026-00617-1 AAV2 capsid clearance and neuronal trafficking dynamics in the central nervous system

Gene Therapy, Published online: 20 April 2026; doi:10.1038/s41434-026-00615-3 Correction: Genetic mutations in HSV-1 replication-defective vectors: Implications for their safety in gene therapy applications

Gene Therapy, Published online: 18 April 2026; doi:10.1038/s41434-026-00612-6 Beneficial bystander-enhanced cryptic splice rescue of cardiac-type Fabry GLA IVS4+919G>A by adenine base editing in patient fibroblasts

Gene Therapy, Published online: 15 April 2026; doi:10.1038/s41434-026-00614-4 Retraction Note: Local administration of transcription factor decoy oligonucleotides to nuclear factor-κB prevents carrageenin-induced inflammation in rat hind paw

Gene Therapy, Published online: 14 April 2026; doi:10.1038/s41434-026-00611-7 CRISPR/Cas9-mediated gene correction of Wilson disease H1069Q point mutation in patient-specific induced pluripotent stem cells

Gene Therapy, Published online: 13 April 2026; doi:10.1038/s41434-026-00613-5 Antimicrobial resistance and gene therapy: emerging molecular strategies for a global health threat

Gene Therapy, Published online: 10 April 2026; doi:10.1038/s41434-026-00610-8 Vaccine elicitation of HIV broadly neutralizing antibodies from genome-edited B cells in non-human primates and derived lymphoid organoids