Personalized Gene Therapy Helps Teen with Rare Form of Severe Epilepsy Walk Independently

The two-year treatment targeting protein production by disease-causing mutations dramatically reduced seizures and sparked developmental gains, helping one teenager walk independently. SAN DIEGO, Calif. — July 21, 2026 – SCN2A‑related developmental epileptic encephalopathy (DEE) is a rare, severe form of childhood epilepsy and one of the most common causes of monogenic autism. The condition is […] The post Personalized Gene Therapy Helps Teen with Rare Form of Severe Epilepsy Walk Independently appeared first on RCIGM .