MMolecular Therapy Advances3/1/2026Optimized AAV Vector Enables Potent Therapeutic Rescue of Inherited Glycosylphosphatidylinositol Deficiency in MiceSaori Umeshita·Yoshiko Murakami·Kathrin Meyer·Shinichi Muramatsu·Kae Imanishi·Mika Ito·Naomi Takino·Taroh Kinoshita·Shibi LikhiteRead at Molecular Therapy AdvancesTagsTrypanosoma species research and implicationsEpidemiology