Preclinical evaluation of INS1201 AAV9-micro-dystrophin via CSF administration as a potential therapy for Duchenne muscular dystrophy
Gretchen M. Thomsen·Brian K. Kaspar·Maiya Lee·Junguo Zhou·Theresa I Slaiwa·Allan Kaspar·Melissa McAlonis‐Downes·Nuria Casanova-Vallve·Hideshi Tsusaki·Samuel R. Ward·Simon Schenk·Jaedyn L. Rollins·Laura Ferraiuolo·Christopher Forespring·Ashley Renteria·Veronica J. Garcia·Ryan Hsu·Tracy TreDenick·Erin Hurley·Akiko Moriyama·Mark Stahl·Michael Molony·Jiaqin Yao·W.David Arnold·Tetsuya Yoshikawa·Catherine Kozial·Marissa Kruger·Samit Varma·Hana Julazadeh·Binh Chu·Ryan Weiss·Robert Cano·Michael Fraser·Shannon N. Bremner·Haunani Bautista·Lynn Bayless