MMolecular Therapy Advances2/18/2026CSF and plasma neuro-biomarker dynamics after gene therapy for cerebral adrenoleukodystrophyT.C. Lund·PJ Orchard·D.R. Nascene·AO Gupta·D.J. Loes·S. KempRead at Molecular Therapy AdvancesTagsPeroxisome Proliferator-Activated ReceptorsMolecular Biology
