Abstract Context X-linked hypophosphatemia (XLH) is a rare, genetic, progressive, lifelong disorder manifest by impaired growth and disproportionate short stature. Burosumab, a monoclonal antibody against fibroblast growth factor 23, is approved for treating patients with XLH. Objective To understand the impact of burosumab treatment on growth in a real-world setting. Design Interim data from three ongoing, real-world observational studies (NCT03651505, NCT03193476, NCT03745521), were unified in
Real-world Impact of Treatment on Growth in Children With X-Linked Hypophosphatemia
Seiji Fukumoto·Thomas O Carpenter·Erik A. Imel·Keiichi Ozono·M L Brandi·Haruka Ishii·Zhiyi Li·Kerry Sandilands·Paul Joos-Vandewalle·Cheuk Yan Lee·Masanori Kanematsu·Keith McCullough·Dieter Haffner
